The Administrative Core is organized to provide support and oversight for the Program Projects. It is designed to facilitate exchange of ideas and scientific interactions among Projects and Cores. Core A will continue to serve as the communication center where our internal and external committees can channel their comments to individual project/core leaders, as well a central place that the Internal and External Advisory Boards can monitor project progression. Core A will keep our internal advisory board (Drs. Bennett, Haskins, June and Wright) and our external advisory board (Drs. Bray, Hedner and Schaub) updated about experimental outcomes on a semi-annual basis. It will provide services to individual projects in areas such as budget control, abstract and manuscript preparation, and meeting scheduling.

National Institute of Health (NIH)
National Heart, Lung, and Blood Institute (NHLBI)
Research Program Projects (P01)
Project #
Application #
Study Section
Heart, Lung, and Blood Initial Review Group (HLBP)
Project Start
Project End
Budget Start
Budget End
Support Year
Fiscal Year
Total Cost
Indirect Cost
Children's Hospital of Philadelphia
United States
Zip Code
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High, Katherine A; Anguela, Xavier M (2016) Adeno-associated viral vectors for the treatment of hemophilia. Hum Mol Genet 25:R36-41
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Sharma, Rajiv; Anguela, Xavier M; Doyon, Yannick et al. (2015) In vivo genome editing of the albumin locus as a platform for protein replacement therapy. Blood 126:1777-84
Nichols, Timothy C; Whitford, Margaret H; Arruda, Valder R et al. (2015) Translational data from adeno-associated virus-mediated gene therapy of hemophilia B in dogs. Hum Gene Ther Clin Dev 26:5-14
Rozenova, Krasimira; Jiang, Jing; Donaghy, Ryan et al. (2015) MERIT40 deficiency expands hematopoietic stem cell pools by regulating thrombopoietin receptor signaling. Blood 125:1730-8
Jain, Deepti; Mishra, Tejaswini; Giardine, Belinda M et al. (2015) Dynamics of GATA1 binding and expression response in a GATA1-induced erythroid differentiation system. Genom Data 4:1-7
Shaham, Lital; Vendramini, Elena; Ge, Yubin et al. (2015) MicroRNA-486-5p is an erythroid oncomiR of the myeloid leukemias of Down syndrome. Blood 125:1292-301

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