The Center for Duchenne Muscular Dystrophy ('CDMD') Core Center provides an academic home to researchers in the Los Angeles area interested in discovery and translafion of therapies in the muscular dystrophies. The Center facilitates innovafion and provides institufional resources for interdisciplinary,. translafional research, by providing its 45 members access to unique core facilities, pilot funding mechanisms, seminars and an annual retreat focused on muscle research. This is an excifing fime in muscular dystrophy research, since for the first fime, several rafionally designed therapeufics are in clinical trials and novel therapeufic pathways have been identified. In this era of translation, the CDMD Core Center is well posifioned to capitalize on the progress that has been made, to identify drugs in novel dystrophyrelevant pathways and bring these drugs to clinical trials. The Administrative and Enrichment core will help to speed progress along these lines by promofing collaborafion and communicafion amongst Center Scientists, managing the Pilot and Feasibility Seed Grant Program, organizing seminars, retreats and group meefings. Aside from the scienfific acfivifies, the Center has strong missions in educafion, clinical care and outreach. The Administrative and Enrichment Core has 6 main goals;
aim 1 : to facilitate communication between Center Scienfists, by providing administrative and website support to the Cores and all acfivifies ofthe Center;
aim 2 : to facilitate collaborafion between Center Scienfists by organizing enrichment acfivifies such as a seminar series, annual retreat and regular working group meefings;
aim 3 : to facilitate collaborafion between CDMD basic scienfists and clinicians in the neuromuscular clinic and to improve clinical care for those suffering with neuromuscular disorders;
aim 4 : to oversee the review and funding ofthe Pilot and Feasibility Seed Grant Program;
aim 5 : to improve the training experience of individuals seeking to develop knowledge and skills in translafional research relevant to muscular dystrophy, by promofing acfivifies that benefit the educafion mission ofthe CDMD;
aim 6 : to engage the community through outreach efforts, by improving disseminafion of informafion about the muscular dystrophies and CDMD events relevant to the public.

National Institute of Health (NIH)
National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)
Center Core Grants (P30)
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Special Emphasis Panel (ZAR1-XZ (M1))
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University of California Los Angeles
Los Angeles
United States
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