Wakamiya, M; Blackburn, M R; Jurecic, R et al. (1995) Disruption of the adenosine deaminase gene causes hepatocellular impairment and perinatal lethality in mice. Proc Natl Acad Sci U S A 92:3673-7
|
Mitani, K; Clemens, P R; Moseley, A B et al. (1993) Gene transfer therapy for heritable disease: cell and expression targeting. Philos Trans R Soc Lond B Biol Sci 339:217-24
|
Grompe, M; Jones, S N; Loulseged, H et al. (1992) Retroviral-mediated gene transfer of human ornithine transcarbamylase into primary hepatocytes of spf and spf-ash mice. Hum Gene Ther 3:35-44
|
Moore, K A; Scarpa, M; Kooyer, S et al. (1991) Evaluation of lymphoid-specific enhancer addition or substitution in a basic retrovirus vector. Hum Gene Ther 2:307-15
|
Cournoyer, D; Scarpa, M; Mitani, K et al. (1991) Gene transfer of adenosine deaminase into primitive human hematopoietic progenitor cells. Hum Gene Ther 2:203-13
|
Jones, S N; Jones, P G; Ibarguen, H et al. (1991) Induction of the Cyp1a-1 dioxin-responsive enhancer in transgenic mice. Nucleic Acids Res 19:6547-51
|
Grompe, M; Mitani, K; Lee, C C et al. (1991) Gene therapy in man and mice: adenosine deaminase deficiency, ornithine transcarbamylase deficiency, and Duchenne muscular dystrophy. Adv Exp Med Biol 309B:51-6
|