The administrative core of this translational program is integral to the Horae Gene Therapy Center (GTC) of UMMS, and provides the mechanism for pre- and post-award administration of the program, for convening of the investigators who constitute the key personnel of the subprojects and cores, and for assembling the External Advisory Committee to provide ongoing peer review and input to all programmatic initiatives. The administrative core interacts at all levels with the central administration of UMMS (including the office of the Provost/Dean, the Office of Research, and the Center for Clinical and Translational Science). Finally, the Administrative core will provide assistance to the communication of results through peer review publications and presentations at national meetings relevant to pulmonary disease, gene therapy, and alpha-1 antitrypsin deficiency, specifically.

Agency
National Institute of Health (NIH)
Institute
National Heart, Lung, and Blood Institute (NHLBI)
Type
Research Program Projects (P01)
Project #
5P01HL131471-05
Application #
9935121
Study Section
Special Emphasis Panel (ZHL1)
Program Officer
Postow, Lisa
Project Start
Project End
Budget Start
2020-05-01
Budget End
2021-04-30
Support Year
5
Fiscal Year
2020
Total Cost
Indirect Cost
Name
University of Massachusetts Medical School Worcester
Department
Type
DUNS #
603847393
City
Worcester
State
MA
Country
United States
Zip Code
01655
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Wang, Dan; Gao, Guangping (2018) Taking a Hint from Structural Biology: To Better Understand AAV Transport across the BBB. Mol Ther 26:336-338

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