Huang, M M; Tsuboi, S; Wong, A et al. (2000) Expression of human Wiskott-Aldrich syndrome protein in patients' cells leads to partial correction of a phenotypic abnormality of cell surface glycoproteins. Gene Ther 7:314-20 |
Huang, M M; Wong, A; Yu, X et al. (1997) Retrovirus-mediated transfer of the human alpha-L-iduronidase cDNA into human hematopoietic progenitor cells leads to correction in trans of Hurler fibroblasts. Gene Ther 4:1150-9 |