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Shapiro, Elsa G; Nestrasil, Igor; Rudser, Kyle et al. (2015) Neurocognition across the spectrum of mucopolysaccharidosis type I: Age, severity, and treatment. Mol Genet Metab 116:61-8
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Bjoraker, Kendra J; Delaney, Kathleen; Peters, Charles et al. (2006) Long-term outcomes of adaptive functions for children with mucopolysaccharidosis I (Hurler syndrome) treated with hematopoietic stem cell transplantation. J Dev Behav Pediatr 27:290-6
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Peters, Charles; Charnas, Lawrence R; Tan, Ye et al. (2004) Cerebral X-linked adrenoleukodystrophy: the international hematopoietic cell transplantation experience from 1982 to 1999. Blood 104:881-8
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Grewal, S S; Krivit, W; Defor, T E et al. (2002) Outcome of second hematopoietic cell transplantation in Hurler syndrome. Bone Marrow Transplant 29:491-6
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Jacobson, P; Park, J J; DeFor, T E et al. (2001) Oral busulfan pharmacokinetics and engraftment in children with Hurler syndrome and other inherited metabolic storage diseases undergoing hematopoietic cell transplantation. Bone Marrow Transplant 27:855-61
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Shapiro, E; Krivit, W; Lockman, L et al. (2000) Long-term effect of bone-marrow transplantation for childhood-onset cerebral X-linked adrenoleukodystrophy. Lancet 356:713-8
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Krivit, W; Peters, C; Dusenbery, K et al. (2000) Wolman disease successfully treated by bone marrow transplantation. Bone Marrow Transplant 26:567-70
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Krivit, W; Shapiro, E G; Peters, C et al. (1998) Hematopoietic stem-cell transplantation in globoid-cell leukodystrophy. N Engl J Med 338:1119-26
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Peters, C; Shapiro, E G; Anderson, J et al. (1998) Hurler syndrome: II. Outcome of HLA-genotypically identical sibling and HLA-haploidentical related donor bone marrow transplantation in fifty-four children. The Storage Disease Collaborative Study Group. Blood 91:2601-8
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Rajanayagam, V; Balthazor, M; Shapiro, E G et al. (1997) Proton MR spectroscopy and neuropsychological testing in adrenoleukodystrophy. AJNR Am J Neuroradiol 18:1909-14
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